Which Drug Will Be the First Approved for Duchenne Muscular Dystrophy?

In Clinical Development by Freya Smale


Four drugs are vying to be 1st approved for treating patients with Duchenne muscular dystrophy (DMD). Of the 4 drugs in late stage development, 3 will only be effective for subsets of the DMD population (10-15%) and 2 of those 3 are for the same subset (exon 51 mutation).  And the 4th drug is being developed to treat all DMD patients but will probably only slow progression of the disease slightly. The other 3 will hopefully deter progression of the disease much longer. But that is just speculation. We still need to see the phase 3 data for all of them.
So which drug will be the first?  – See more at: http://www.raredr.com/front-page-legislation/articles/which-orphan-drug-will-be-first-approved-duchenne-muscular-dystrop-0#sthash.d2EobOGg.dpuf

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