Zohar Argov of BioBlast Pharma joined us for World Orphan Drug Congress USA 2015 to present about ‘ Developing a mutant protein-stabilizing platform based on a small molecule for orphan diseases’
Download the presentation now to learn about:
- Trehalose as a known protein stabilizer and autophagy enhancer
- Proof of Concept: Trehalose in OPMD
- Current human studies of Cabaletta
…and much more!
Get your copy here !
To learn more about developing a mutant protein-stabilizing platform , attend World Orphan Drug Congress USA 2016 September 2-3 in Washington, DC.